A 19-year-old Canadian man becomes the first human cured through prime gene editing after doctors corrected a rare genetic ...

Prime Medicine's application will test an FDA that has promised to speed new gene-editing treatments but has recently spurned ...

After teasing a new regulatory process for personalized genetic medicines at the end of last year, the FDA today unveiled draft guidance for an approval pathway that could see custom CRISPR therapies, ...

The FDA proposes new rules allowing mutation-specific gene therapies to qualify for approval despite extremely small patient ...

Gene editing, a set of techniques used to alter sections of an organism's DNA, is helping scientists cure diseases previously ...

Researchers have found that a new base-editing gene therapy can help treat a rare neurodevelopmental disorder called Snijders ...

We are in the golden age of science and technology, advancements in gene editing and ASO therapies are allowing doctors to deliver targeted, and in some cases one-time, interventions for conditions ...

UCLA researchers use lipid nanoparticles to insert full CFTR gene into airway cells, restoring function and opening new avenues for CF therapy.

Better mRNA release inside cells boosts vaccine and gene editing performance, enabled by redesigned lipid molecules that grip ...

"Gene editing takes centre stage in FDA’s new rare disease approval pathway" was originally created and published by ...

Gene-edited animals, including faster-growing fish, heat-tolerant cows and disease-resistant pigs, have already been approved in the United States, Japan and several countries in South America. These ...

Editas Medicine Inc. (NASDAQ:EDIT) reported fourth-quarter results that came in ahead of analyst expectations, with the ...